CAMP4 Therapeutics Corp

NASDAQ:CAMPUnited States

CAMP4 Therapeutics Corporation is a clinical-stage biopharmaceutical company pioneering the discovery and development of regulatory RNA-based therapeutics with the goal of upregulating gene expression and restoring healthy protein levels to treat a broad range of genetic diseases. It is leveraging its RAP Platform to advance a pipeline of programs initially focused on metabolic and central nervous system (CNS) disorders with validated disease biology and potential market opportunities due to the significant unmet need of affected patients. Its lead product candidate, CMP-CPS-001, has the potential to be the first disease-modifying therapy for the treatment of urea cycle disorders. CMP-CPS-001 is designed to improve urea cycle activity by amplifying expression of CPS1, a key enzyme that catalyzes the first step of the urea cycle, by binding to a CPS1-specific regRNA. Its CNS development program, CMP-SYNGAP, is focused on addressing the underlying cause of SYNGAP1-related disorders.

Contact Information

Headquarters

One Kendall Square Bldg 1400 West 3rd FloorCAMBRIDGE, MA, United States 02139

Phone

617-651-8867

Fax

302-655-5049

Executives

Independent Chairman of the Board

Steven Holtzman

President, Chief Executive Officer, Director

Josh Mandel-Brehm

Chief Financial Officer

Kelly Gold

Chief Scientific Officer, Senior Vice President of Research

David Bumcrot

Chief Medical Officer

Yuri Maricich